A mouse study suggests SMA treatment may partly restore organ-specific redox imbalances linked to SMN protein deficiency.

Access to timely treatment for spinal muscular atrophy (SMA) remains a challenge, with barriers including delays in diagnosis, frequent treatment needs, and insurance coverage gaps, which impact ...

Early treatment helps with swallowing and eating for SMA kids, but new research is needed on the effects of disease-modifying ...

ZURICH (Reuters) - Novartis's gene therapy for spinal muscular atrophy (SMA) could be approved in May 2019 after the U.S. Food and Drug Administration agreed to an accelerated review of the Swiss ...

Panelists discuss how the current spinal muscular atrophy (SMA) treatment landscape includes 3 options: gene therapy (onasemnogene abeparvovec [Zolgensma]) for younger patients and 2 splice modifiers ...

"More domestic patients with spinal muscular atrophy (SMA) will have the opportunity for drug treatment in the future." Biogen Korea held its first press conference on the 2nd at the Conrad Seoul ...

Thiruvananthapuram: For the first time in India, pre-symptomatic treatment to an infant, diagnosed with spinal muscular atrophy (SMA) within days of birth, was provided in Kerala, marking a ...

When Jesy Nelson revealed that her twin daughters, Ocean Jade and Story ...

The Kerala model is crucial as SMA patients in India had a long wait for a viable treatment option. Kindly note the image has been posted only for representational purposes. Photograph: Kind courtesy ...